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Severe Combined Immunodeficiency - 33 Studies Found
Estado | Estudiar |
Not yet recruiting |
Nombre del estudio: Safety and Early Efficacy Study of TBX-1400 in Patients With Severe Combined Immunodeficiencies Condición: Severe Combined Immunodeficiency Fecha: 2016-07-26 Intervenciones: Biological: TBX-1400 |
Completed |
Nombre del estudio: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome Condición: Severe Combined Immunodeficiency Fecha: 2005-09-07 Intervenciones:
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Active, not recruiting |
Nombre del estudio: Generalized Neonatal Screening of Severe Combined Immunodeficiencies Condición: Severe Combined Immunodeficiency, Atypical Fecha: 2014-09-02 Intervenciones: Biological: SCID screening |
Active, not recruiting |
Nombre del estudio: Clinical Characteristics and Genetic Profiles of Severe Combined Immunodeficiency in China Condición: Severe Combined Immunodeficiency Fecha: 2014-09-01 Intervenciones: Genetic: gene sequencing Amplify and identify exons from gene IL-2RG by PCR and agarose gel electrophore |
Completed |
Nombre del estudio: Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID) Condición: Severe Combined Immunodeficiency Fecha: 2001-12-17 Intervenciones: Drug: Gene-Transduced Autologous CD34+ Stem Cells |
Active, not recruiting |
Nombre del estudio: Gene Therapy for X-linked Severe Combined Immunodeficiency Condición: X-linked Severe Combined Immunodeficiency Fecha: 2011-06-21 Intervenciones: Other: Gene transfer Single infusion of autologous CD34+ cells transduced with the self-inactivating (SI |
Recruiting |
Nombre del estudio: Neonatal Screening of Severe Combined Immunodeficiencies Condición:
Fecha: 2015-10-27 |
Recruiting |
Nombre del estudio: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants Condición: Severe Combined Immunodeficiency Disease, X-linked Fecha: 2012-01-13 Intervenciones:
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Completed |
Nombre del estudio: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study Condición: Severe Combined Immunodeficiency Fecha: 1999-11-03 Intervenciones:
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Recruiting |
Nombre del estudio: Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector Condición: Severe Combined Immunodeficiency Fecha: 2010-05-21 Intervenciones: Biological: Gene transfer Three procedures: 1) Bone marrow harvest from the patient's posterior iliac cr |